| Therapeutic agent for glycogen storage disease type iii |
2023-3-13 |
2023-5-30 |
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| Certain dux4 inhibitors and methods of use thereof |
2023-2-27 |
2023-9-07 |
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| Solid compositions of triglycerides and uses thereof |
2023-2-10 |
2023-6-15 |
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| Engineered cell lines for increased production of recombinant adeno-associated … |
2022-10-28 |
2023-5-04 |
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| Methods of using anti-sclerostin antibodies in treatment of osteogenesis … |
2022-9-29 |
2023-4-06 |
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| Methods and compositions for the treatment of amyloidosis |
2022-9-06 |
2023-4-27 |
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| Methods of heat inactivation of adenovirus |
2022-8-25 |
2022-11-01 |
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| Recombinant aav formulations |
2022-8-18 |
2023-2-23 |
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| Anion-exchange chromatography methods for purification of recombinant adeno- … |
2022-8-17 |
2023-2-23 |
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| Compositions and methods for treating a muscular dystrophy |
2022-8-10 |
2023-2-16 |
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| Gene therapy for treating cdkl5 deficiency disorder |
2022-7-14 |
2022-9-01 |
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| Creatine prodrugs, compositions and methods of use thereof |
2022-3-28 |
2022-7-21 |
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| Creatine prodrugs, compositions and methods of use thereof |
2022-3-28 |
2023-9-12 |
2023-9-12 |
| Compositions and methods for treatment of hemochromatosis |
2021-11-25 |
2022-1-01 |
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| Effective and efficient control of serum phosphate for optimal bone formation |
2021-11-12 |
2022-5-05 |
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| Sialylated glycoprotein compositons and uses thereof |
2021-11-11 |
2022-6-30 |
|
| Genetically Engineered Producer Cell Lines and Methods of Making and Using Them |
2021-10-14 |
2021-10-29 |
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| DUX4 INHIBITORS AND METHODS OF USE THEREOF |
2021-9-01 |
2022-11-30 |
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| Gene therapy constructs for the treatment of Wilson's disease |
2021-7-29 |
2021-9-20 |
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| Methods and compositions for treating glycogen storage diseases |
2021-6-13 |
2021-7-29 |
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| GENE THERAPY TO TREAT PROPIONIC ACIDEMIA |
2021-3-31 |
2022-6-29 |
|
| Compositions and methods for reducing reverse packaging of cap and rep … |
2021-3-19 |
2023-1-25 |
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| METHODS TO ENHANCE THE YIELD OF RECOMBINANT ADENO-ASSOCIATED VIRUSES |
2021-3-15 |
2022-12-20 |
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| GENE THERAPY FOR THE TREATMENT OF CDKL5 DEFICIENCY DISORDER |
2021-2-12 |
2022-9-07 |
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| Chaotropic agents for reducing double stranded RNA formation |
2021-2-04 |
2022-9-20 |
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| Methods for improved therapeutic use of recombinant aav |
2020-10-01 |
2022-11-03 |
|
| COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOCHROMASIS |
2020-5-22 |
2021-11-17 |
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| GENOMODIFIED PRODUCER CELLULAR STRAPS AND METHODS TO MAKE THEM AND USE THEM |
2020-4-08 |
2021-10-20 |
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| GENE THERAPY CONSTRUCTIONS FOR THE TREATMENT OF WILSON'S DISEASE |
2020-1-03 |
2021-8-25 |
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| Gene therapy for treating propionic acidemia |
2019-10-01 |
2021-6-11 |
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| Sialic acid analogs |
2019-9-16 |
2021-1-12 |
2021-1-12 |
| Therapeutics for phenylketonuria |
2018-5-31 |
2018-12-06 |
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| Scalable method for producing transfection reagents |
2018-5-09 |
2020-4-23 |
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| Cell culture methods involving hdac inhibitors or rep proteins |
2018-3-22 |
2020-1-30 |
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| Methods for enhancing yield of recombinant adeno-associated virus |
2018-3-22 |
2020-2-13 |
|
| Compositions and methods for treatment of movement disorders |
2018-1-23 |
2018-5-31 |
|
| Use of tonicifying agents to enhance recombinant adeno-associated virus yield |
2017-10-13 |
2021-9-09 |
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| Method and formulation for treating sialic acid deficiency |
2017-7-21 |
2017-10-12 |
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| Use of glucocorticoid analogs to enhance recombinant adeno-associated virus … |
2017-7-12 |
2019-12-25 |
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| Methods and formulations for treating sialic acid deficiencies |
2016-12-19 |
2017-6-08 |
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| CRYSTAL FORMS OF SYALIC ACID OR A SALT OR SOLVATE OF THIS |
2016-9-14 |
2017-12-06 |
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| Creatine prodrugs, compositions and methods of use thereof |
2015-12-22 |
2016-8-16 |
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| COMPOSITIONS OF SUCCESSFUL GLICOPROTEINS AND USES OF THESE |
2015-3-05 |
2016-8-10 |
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| COMPOSITION, PHARMACEUTICAL COMPOSITION AND THEIR USE |
2014-11-14 |
2023-7-04 |
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| Creatine analogs and the use thereof |
2014-11-05 |
2015-5-14 |
|
| Biomarkers for assessing treatment of sialic acid deficiency diseases and … |
2013-9-20 |
2014-3-27 |
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| Methods and formulations for treating sialic acid deficiencies |
2012-10-24 |
2013-5-02 |
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| Biomarkers for assessing sialic acid deficiencies |
2011-12-16 |
2012-11-01 |
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| Certains inhibiteurs dux4 et leurs procédés d'utilisation |
2023-2-27 |
2023-9-07 |
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| Composição, composição farmacêutica e uso das mesmas |
2014-11-14 |
2023-7-04 |
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