| Use of histidine rich peptides as a transfection reagent for raav and rbv … |
2023-7-30 |
2023-9-01 |
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| Novel adeno-associated virus capsid proteins |
2023-4-04 |
2023-6-01 |
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| Use of C-type natriuretic peptide variants to treat skeletal dysplasia |
2023-2-08 |
2023-4-27 |
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| ADENO-ASSOCIATED VIRUS VECTORS HAVING A FACTOR VIII GENE |
2023-2-02 |
2023-3-24 |
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| C-type natriuretic peptide therapy of bone-related disorders |
2022-12-07 |
2023-6-15 |
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| Glycolate oxidase inhibitors for the treatment of disease |
2022-10-30 |
2022-12-01 |
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| Adeno-associated virus factor viii vectors, associated viral particles and … |
2022-10-18 |
2022-12-01 |
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| Treatment of hereditary angioedema with aav gene therapy vectors and … |
2022-9-30 |
2023-5-11 |
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| Cyclic glycolate oxidase inhibitor compounds for the treatment of diseases (div … |
2022-9-05 |
2023-3-17 |
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| Cyclic glycolate oxidase inhibitor compounds for the treatment of diseases (div … |
2022-9-05 |
2023-3-17 |
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| Aav capsid compositions and methods for delivery |
2022-9-02 |
2023-3-09 |
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| Aav capsid compositions and methods for delivery |
2022-9-02 |
2023-3-09 |
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| Aav capsid compositions and methods for delivery |
2022-9-02 |
2023-3-09 |
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| Aav capsid compositions and methods for delivery |
2022-9-02 |
2023-3-09 |
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| Aav capsid compositions and methods for delivery |
2022-9-02 |
2023-3-09 |
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| Lysosomal Targeting Peptides and Uses Thereof |
2022-7-27 |
2023-8-03 |
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| Large scale adeno-associated virus production systems |
2022-7-27 |
2023-3-16 |
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| C-Type Natriuretic Peptide Variants to Treat Skeletal Dysplasia in Children |
2022-7-11 |
2023-5-04 |
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| Cell culture feed for recombinant adeno-associated virus production in … |
2022-6-29 |
2023-1-05 |
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| Compositions of beta-hexosaminidase variants and uses thereof |
2022-6-24 |
2022-12-29 |
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| Compositions of prokaryotic phenylalanine ammonia-lyase and methods of treating … |
2022-5-18 |
2022-11-24 |
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| Treatment of hereditary angioedema with liver-specific gene therapy vectors |
2022-5-13 |
2023-3-10 |
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| Targeted therapeutic lysosomal enzyme fusion proteins, associated formulations … |
2022-4-25 |
2022-8-11 |
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| CNP variants and their conjugates |
2022-4-05 |
2022-8-30 |
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| Characterization of gene therapy viral particles using size exclusion … |
2022-3-03 |
2022-5-01 |
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| Methods for the treatment of cln2 disease in pediatric subjects |
2022-2-28 |
2022-10-21 |
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| Hydrophobic peptide salts for extended release compositions |
2022-2-09 |
2022-4-01 |
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| Vosoritide in all forms protected by the basic patent |
2022-2-01 |
2022-2-01 |
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| Aav production systems for aav viral particles with improved infectivity |
2022-1-28 |
2022-12-01 |
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| C-TYPE NATRIURETIC PEPTIDE VARIANTS |
2022-1-28 |
2023-1-13 |
2023-1-13 |
| Targeted Therapeutic Lysosomal Enzyme Fusion Proteins and Uses Thereof |
2022-1-10 |
2022-4-28 |
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| Glycolate oxidase inhibitors for the treatment of diseases |
2021-12-16 |
2022-9-23 |
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| Use of c-type natriuretic peptide variants to treat osteoarthritis |
2021-12-03 |
2022-5-26 |
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| Process for enriching adeno-associated virus |
2021-11-02 |
2022-5-05 |
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| Oligonucleotide |
2021-9-29 |
2022-3-31 |
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| Tpp-1 formulations and methods for treating cln2 disease |
2021-8-13 |
2021-11-04 |
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| Use of regulatory proteins for the production of adeno-associated virus |
2021-5-20 |
2021-12-30 |
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| Treatment of phenylketonuria with aav and therapeutic formulations |
2021-4-02 |
2021-10-07 |
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| Treatment of fabry disease with aav gene therapy vectors |
2021-3-12 |
2021-9-16 |
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| Manufacture of active highly phosphorylated human lysosomal sulfatase enzymes … |
2021-3-01 |
2021-6-24 |
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| Tetrahydrobiopterin for treating conditions associated with elevated … |
2021-2-11 |
2021-4-02 |
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| Histone deacetylase inhibitors |
2021-2-11 |
2021-4-29 |
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| Virus-free cell cultures |
2021-2-09 |
2023-3-09 |
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| C-TYPE NATRIURETIC PEPTIDE VARIANTS |
2020-12-29 |
2022-3-30 |
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| TREATMENT OF HEREDITARY ANGIOEDEMA WITH LIVER-SPECIFIC GENE THERAPY VECTORS |
2020-11-13 |
2022-2-16 |
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| Secondary container with flow-through apertures for freezing, thawing, and … |
2020-11-13 |
2021-5-20 |
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| New adeno-associated viral vectors targeting the liver |
2020-11-13 |
2021-4-30 |
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| Phenylketonuria Treatment Methods |
2020-11-06 |
2021-5-07 |
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| Histone deacetylase inhibitors |
2020-9-22 |
2021-1-14 |
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| VARIANTS OF CNP AND ITS CONJUGATES |
2020-9-16 |
2022-8-31 |
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| HYDROPHOBIC PEPTIDE SALTS FOR PROLONGED-RELEASE COMPOSITIONS |
2020-8-12 |
2022-8-31 |
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| Hydrophobic peptide salts for extended release compositions incorporation by … |
2020-8-12 |
2021-6-01 |
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| PRODUCTION OF A HIGHLY PHOSPHORYLATED ACTIVE HUMAN N-ACETYGALACTOSAMINE-6- … |
2020-7-31 |
2021-12-29 |
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| GLYCOLATE OXIDASE INHIBITORS FOR THE TREATMENT OF A DISEASE |
2020-6-18 |
2021-12-01 |
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| Methods of redosing gene therapy vectors |
2020-5-13 |
2020-11-19 |
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| Methods of diagnosing a disease and methods of monitoring treatment of a … |
2020-5-08 |
2021-1-28 |
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| Detection of oligosaccharides |
2020-5-04 |
2021-1-21 |
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| A RECOMBINANT HUMAN N-ACETYLGALACTOSAMINE-6-SULFATASE (GALNS) ENZYME, … |
2020-2-20 |
2021-9-22 |
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| Dihydropyridophthalazinone inhibitors of poly(adp-ribose)polymerase (parp) |
2019-12-13 |
2020-8-20 |
|
| Compositions of prokaryotic phenylalanine ammonia-lyase and methods of using … |
2019-10-18 |
2019-11-28 |
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| Hdac inhibitors |
2019-8-22 |
2019-12-19 |
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| Glucosylceramide synthase inhibitors for the treatment of diseases |
2019-7-29 |
2019-9-26 |
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| Ceramide galactosyltransferase inhibitors for the treatment of disease |
2019-7-29 |
2020-2-06 |
|
| Stable expression of aav vectors in juvenile subjects. |
2019-5-14 |
2022-7-13 |
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| METHODS TO TREAT PHENYLKETONURIA |
2019-5-08 |
2021-8-18 |
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| Targeted Therapeutic Proteins |
2019-4-09 |
2019-7-25 |
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| Histone deacetylase inhibitors |
2019-3-12 |
2021-4-20 |
2021-4-20 |
| Quantification of non-reducing end glycan residual compounds for determining … |
2019-2-20 |
2019-8-15 |
|
| N-(1-hydroxy-3-(pyrrolidinyl)propan-2-yl)pyrrolidine-3-carboxamide derivatives … |
2019-2-12 |
2022-6-14 |
2022-6-14 |
| Dry blend formulation of tetrahydrobiopterin |
2019-1-31 |
2019-5-30 |
|
| Glucosylceramide synthase inhibitors for the treatment of diseases |
2019-1-18 |
2020-9-01 |
2020-9-01 |
| Compositions of prokaryotic phenylalanine ammonia-lyase variants and methods of … |
2019-1-11 |
2022-11-22 |
2022-11-22 |
| QUANTIFICATION OF NON-REDUCING NON-REDUCING END COMPONENTS |
2019-1-07 |
2019-12-11 |
|
| Histone deacetylase inhibitors |
2018-12-26 |
2019-4-25 |
|
| Ceramide galactosyltransferase inhibitors for the treatment of disease |
2018-11-20 |
2019-5-31 |
|
| Cell-based assays for detection of antibodies or other factors that neutralize … |
2018-10-05 |
2019-6-21 |
|
| Dihydropyridophthalazinone inhibitors of poly(ADP-ribose)polymerase (PARP) for … |
2018-8-03 |
2019-12-03 |
2019-12-03 |
| Methods and compositions for the treatment of metabolic disorders |
2018-5-08 |
2018-9-13 |
|
| Improved lentiviruses for transduction of hematopoietic stem cells |
2018-5-03 |
2021-5-13 |
|
| Histone deacetylase inhibitors |
2017-12-22 |
2019-8-29 |
|
| Ceramide galactosyltransferase inhibitors for the treatment of disease |
2017-12-19 |
2018-6-28 |
|
| For targeting the substance of various selected organs or tissue |
2017-11-15 |
2019-9-20 |
|
| Crystalline (8S,9R)-5-fluoro-8-(4-fluorophenyl)-9-(1-methyl-1H-1,2,4-triazol-5- … |
2017-7-17 |
2019-1-29 |
2019-1-29 |
| Ceramide galactosyltransferase inhibitors for the treatment of disease |
2017-6-09 |
2017-12-14 |
|
| Heparan sulfate biosynthesis inhibitors for the treatment of diseases |
2017-4-28 |
2018-4-25 |
|
| Delivery of Therapeutic Compounds to the Brain and Other Tissues |
2017-1-06 |
2017-6-29 |
|
| PHYNYLANINE AMMONIA PRESCRIPTION LYSES COMPOSITIONS AND METHODS OF CANCER … |
2016-11-10 |
2017-6-28 |
|
| VECTORS OF THE FACTOR VIII OF ADENOASOCIATED VIRUSES, ASSOCIATED VIVIC … |
2016-9-23 |
2017-12-13 |
|
| Methods of using inhibitors of pikfyve for the treatment of lysosomal storage … |
2016-9-02 |
2017-3-09 |
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| USE OF TYPE C NATRIURETIC PEPTIDE VARIANTS TO TREAT SKELETTIC DYSPLASIA |
2016-8-01 |
2017-10-18 |
|
| Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of … |
2016-7-15 |
2017-2-16 |
|
| FORMULATIONS OF TRIPEPTIDIL PEPTIDASA 1 (TPP1) AND METHODS OF TREATMENT OF A … |
2016-5-06 |
2017-7-26 |
|